We’re committed to helping rare disease patients irrespective of their ability to pay for treatment. This is written into the constitutional documents of our company, and we’ve been running a Free Goods Programme since 2018.
A Free Goods Programme is a compliant way for medicines that are not approved in their country of intended use to be made available for patients who either have no alternative treatment option or have exhausted all other treatment options available in their country of residence.
Our Free Goods Programme is currently available to patients with Hereditary Tyrosinemia Type 1 (HT-1) and Alkaptonuria (AKU) who live in countries where it is unlikely that they will have the means to pay for rare disease medication, including Argentina, Bangladesh, Brazil, Chile, Colombia, Dominican Republic, India, Jordan, Mexico, Nigeria, Pakistan, Peru, Sudan, Tunisia and Turkey.
HT-1 and AKU are both ultra-rare diseases, and they are both diseases that patients have for life. They can be treated with nitisinone, in combination with dietary restriction of tyrosine and phenylalanine.
We aim to provide nitisinone to 100 patients on the Free Goods Programme and are committed to providing it to these patients for free, for the duration of their life.